MSN: Common gene variant may raise Alzheimer’s risk; researchers eye gene therapy
NPR: Gene therapy for a rare type of deafness shows lasting results
Researchers say a gene therapy allowed deaf children and adults as old as 32 to hear for the first time. The benefits have persisted for more than two years for some patients.
GEN - Genetic Engineering and Biotechnology News: Gene Therapy Briefs: Regeneron Wins FDA Approval for First Neurosensory Gene Therapy
The FDA has granted accelerated approval to Regeneron Pharmaceuticals’ Otarmeni™ (lunsotogene parvec-cwha) as the first gene therapy designed to restore a neurosensory function to normal levels.
Gene Therapy Briefs: Regeneron Wins FDA Approval for First Neurosensory Gene Therapy
BioSpace: Gene therapy leaders aim to help more Baby KJs with novel regulatory models
As cell and gene therapy leaders gathered in Maryland to discuss accelerating clinical trials in children, one “cutting edge” session focused on the need to expedite more bespoke gene editing ...
Gene therapy leaders aim to help more Baby KJs with novel regulatory models
Vox on MSN: Some deaf children are hearing again because of a new gene therapy
Some deaf children are hearing again because of a new gene therapy
CNN on MSN: FDA approves first gene therapy for inherited deafness, shown to restore hearing for children with rare condition
The US Food and Drug Administration on Thursday approved the first gene therapy for inherited hearing loss, a one-time treatment that proved to be life-changing for a small number of children in a ...
FDA approves first gene therapy for inherited deafness, shown to restore hearing for children with rare condition
Scientific American: How a vision-restoring gene therapy proved that we can treat inherited diseases
Three 2026 Breakthrough Prize winners reflect on developing Luxturna, a gene therapy that treats blindness caused by rare inherited eye diseases ...
How a vision-restoring gene therapy proved that we can treat inherited diseases
FierceBiotech: Regenxbio posts clean safety profile for DMD gene therapy as pivotal data loom
Regenxbio has guided its Duchenne muscular dystrophy (DMD) gene therapy candidate through another test, reporting a clean safety profile and functional improvements as it heads toward pivotal data.
Regenxbio posts clean safety profile for DMD gene therapy as pivotal data loom
The idea behind intra-articular gene therapy for treating osteoarthritis (OA) is to deliver the gene-altering vector or cells directly to the precise site of the disease with a single injection — so ...
NPR: The FDA gives the green light to the first gene therapy for deafness
The FDA gives the green light to the first gene therapy for deafness
The American Journal of Managed Care: Gene Expression Profile Helps Predict Atopic Dermatitis Therapy Response
A pioneering gene therapy could help treat a rare seizure disorder called Dravet syndrome, according to new clinical trial results. The drug, called zorevunersen, holds promise, especially for people ...
New Scientist: First ever inhalable gene therapy for cancer gets fast-tracked by FDA
A first-of-its-kind inhalable gene therapy for lung cancer that genetically modifies people’s lung cells has been fast-tracked towards potential approval after promising clinical trial results. “Very ...
An experimental gene therapy appears safe and highly effective for restoring hearing to people born with a rare form of deafness, researchers reported Wednesday. The study, the largest and longest to ...
A genetic variant carried by at least one-fifth of the population may do far more than raise the odds of developing Alzheimer’s disease. New research argues that inheriting two copies of the APOE4 ...
FiercePharma: Regeneron ushers in new genetic medicine era with groundbreaking gene therapy approval
Regeneron ushers in new genetic medicine era with groundbreaking gene therapy approval
The New York Times: New Gene Therapy Enables Children With a Rare Form of Deafness to Hear
New Gene Therapy Enables Children With a Rare Form of Deafness to Hear
We define a gene as a DNA sequence that is transcribed. This definition includes genes that do not encode proteins (not all transcripts are messenger RNA). The definition normally excludes regions of the …
Genes are segments of DNA that give your cells instructions for specific traits or body functions. Different versions of the same gene are called alleles.
gene, unit of hereditary information that occupies a fixed position (locus) on a chromosome. Genes achieve their effects by directing the synthesis of proteins. In eukaryotes (such as animals, …
Genes are specific sections of DNA that have instructions for making proteins. Proteins make up most of the parts of your body and make your body work the right way. You have two copies of every gene. You …
The gene is considered the basic unit of inheritance. Genes are passed from parents to offspring and contain the information needed to specify physical and biological traits.
What is a gene? A gene is the basic physical and functional unit of heredity. Genes are made up of DNA. Some genes act as instructions to make molecules called proteins, which are needed …
A gene is a segment of DNA that contains instructions for building one or more molecules that help the body work. Researchers estimate that humans have about 20,000 genes, which account …
Genes are made up of sequences of DNA and are arranged, one after another, at specific locations on chromosomes in the nucleus of cells.
A gene is a specific stretch of DNA that carries the instructions for making one particular protein or performing one particular function. Humans have roughly 19,400 protein-coding genes, but …
Gene is dedicated to advancing understanding of genes and genomes, including their regulation, expression, function, and evolution, and their roles in biological processes, phenotypes, and diseases …
The knowledgebase automatically integrates gene-centric data from ~200 web sources, including genomic, transcriptomic, proteomic, genetic, clinical and functional information.
Genes are the basic units that determine the traits that we inherit from our parents. 1 They contain coded information found in nearly every cell of the human body. Our genes are made up of …
The treatment, developed by Regeneron Pharmaceuticals, is for a very rare form of deafness. But it represents a medical milestone.